The present invention relates to a nucleic acid construct allowing to drives the expression of a transcription factor in rod cells or cone cells thereby silencing the expression of a gene which mutated form is responsible for a retinal dystrophy and its medical use, relative expression 5 vector, host cell, viral particle and pharmaceutical composition.
ECTOPICALLY EXPRESSED TRANSCRIPTION FACTORS AND USES THEREOF / Surace, Enrico Maria. - (2018).
ECTOPICALLY EXPRESSED TRANSCRIPTION FACTORS AND USES THEREOF
Enrico Maria Surace
Conceptualization
2018
Abstract
The present invention relates to a nucleic acid construct allowing to drives the expression of a transcription factor in rod cells or cone cells thereby silencing the expression of a gene which mutated form is responsible for a retinal dystrophy and its medical use, relative expression 5 vector, host cell, viral particle and pharmaceutical composition.File in questo prodotto:
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