SURACE, Enrico Maria
SURACE, Enrico Maria
DIPARTIMENTO DI SCIENZE MEDICHE TRASLAZIONALI
Adeno-associated viral vectors for retinal gene transfer.
2003 Surace, Enrico Maria; Auricchio, Alberto
The distribution, concentration, and toxicity of enhanced green fluorescent protein in retinal cells after genomic or somatic (virus-mediated) gene transfer.
2005 Rex, Ts; Peet, Ja; Surace, Enrico Maria; Calvert, Pd; Nikonov, Ss; Lyubarsky, Al; Bendo, E; Hughes, T; Pugh EN, Jr; Bennett, J.
Localization of pigment epithelium derived factor (PEDF) in developing and adult human ocular tissues.
2001 Karakousis, Pc; John, Sk; Behling, Kc; Surace, Enrico Maria; Smith, Je; Hendrickson, A; Tang, Wx; Bennett, J; Milam, Ah
Pigment epithelium-derived factor expression in the developing mouse eye.
2002 Behling, Kc; Surace, Enrico Maria; Bennett, J.
Expression pattern of the ocular albinism type 1 (Oa1) gene in the murine retinal pigment epithelium.
2000 Surace, Enrico Maria; Angeletti, B; Ballabio, Andrea; Marigo, V.
Oa1 knock-out: new insights on the pathogenesis of ocular albinism type 1
2000 Incerti, B; Cortese, K; Pizzigoni, A; Surace, Enrico Maria; Varani, S; Coppola, M; Jeffery, G; Seeliger, M; Jaissle, G; Bennett, Dc; Marigo, V; Schiaffino, Mv; Tacchetti, C; Ballabio, Andrea
The ocular albinism type 1 (OA1) protein, an intracellur G protein-coupled receptor, regulates melanosome transport in pigment cells.
2008 Palmisano, I; Bagnato, P; Palmigiano, A; Innamorati, P; Rotondo, G; Altimare, D; Venturi, C; Sviderskaya, Ev; Piccirillo, R; Coppola, M; Marigo, V; Incerti, B; Ballabio, Andrea; Surace, Enrico Maria; Tacchetti, C; Bennett, Dc; Schiaffino, M. V.
AAV vectors efficiently and stably transduce fetal retina.
2003 Surace, Enrico Maria; Auricchio, Alberto; Reich, S. J.; Rex, T.; Glover, E.; Pineles, S.; Tang, W.; O’Connor, E.; Lyubarsky, A.; Savchenko, A.; Pugh, E.; Maguire, A. WILSON J. M. BENNETT J.
Oa1 knock-out: new insights on the pathogenesis of ocular albinism type 1.
2000 Incerti, B; Cortese, K; Pizzigoni, A; Surace, Enrico Maria; Varani, S; Coppola, M; Jeffery, G; Seeliger, M; Jaissle, G; Bennett, Dc; Marigo, V; Schiaffino, Mv; Tacchetti, C; Ballabio, Andrea
SLC7A8, a gene mapping within the lysinuric protein intolerance critical region, encodes a new member of the glycoprotein-associated amino acid transporter family.
1999 Bassi, Mt; Sperandeo, Mp; Incerti, B; Bulfone, A; Pepe, A; Surace, Enrico Maria; Gattuso, C; De Grandi, A; Buoninconti, A; Riboni, M; Manzoni, M; Andria, G; Ballabio, Andrea; Borsani, G; Sebastio, G.
GENE THERAPY FOR LEBER'S CONGENITAL AMAUROSIS IS SAFE AND EFFECTIVE 1.5 YEARS AFTER VECTOR ADMINISTRATION
2010 F., Simonelli; A. M., Maguire; F., Testa; E. A., Pierce; F., Mingozzi; J. L., Bennicelli; S., Rossi; K., Marshall; S., Banfi; Surace, Enrico Maria; J., Sun; T. M., Redmond; X., Zhu; K. S., Scindler; G. S., Ying; C., Ziviello; C., Acerra; J. F., Wright; J. W., Mcdonnell; K. A., High; J., Bennett; Auricchio, Alberto
Recombinant vectors based on porcine adeno-associated viral serotypes transduce the murine and pig retina.
2013 Puppo, A; Bello, A; Manfredi, A; Cesi, G; Marrocco, E; Della Corte, M; Rossi, S; Giunti, M; Bacci, Ml; Simonelli, F; Surace, Enrico Maria; Kobinger, Gp; Auricchio, Alberto
Molecular and clinical characterization of albinism in a large cohort of Italian patients.
2011 Gargiulo, A; Testa, F; Rossi, S; Di Iorio, V; Fecarotta, S; DE BERARDINIS, Teresa; Iovine, A; Magli, A; Signorini, S; Fazzi, E; Galantuomo, Ms; Fossarello, M; Montefusco, S; Ciccodicola, A; Neri, A; Macaluso, C; Simonelli, F; Surace, Enrico Maria
Three-year follow-up after unilateral subretinal delivery of adeno-associated virus in patients with Leber congenital Amaurosis type 2.
2013 Testa, F; Maguire, Am; Rossi, S; Pierce, Ea; Melillo, P; Marshall, K; Banfi, S; Surace, Enrico Maria; Sun, J; Acerra, C; Wright, Jf; Wellman, J; High, Ka; Auricchio, Alberto; Bennett, J; Simonelli, F.
The long noncoding RNA Vax2os1 controls the cell cycle progression of photoreceptor progenitors in the mouse retina.
2012 Meola, N; Pizzo, M; Alfano, G; Surace, Enrico Maria; Banfi, S.
Delivery of adeno-associated virus vectors to the fetal retina: impact of viral capsid proteins on retinal neuronal progenitor transduction.
2003 Surace, Enrico Maria; Auricchio, Alberto; Reich, Sj; Rex, T; Glover, E; Pineles, S; Tang, W; O'Connor, E; Lyubarsky, A; Savchenko, A; Pugh EN, Jr; Maguire, Am; Wilson, Jm; Bennett, J.
Systemic but not intraocular Epo gene transfer protects the retina from light- and genetic-induced degeneration.
2004 Rex, T. S.; M. ALLOCCA, M.; Domenici, L.; Surace, Enrico Maria; Maguire, A. M.; Lyubarsky, A.; Cellerino, A.; Bennett, J.; Auricchio, Alberto
SLC7A8, a gene mapping within the lysinuric protein intolerance critical region, encodes a new member of the glycoprotein associated amino acid transporter family.
1999 Bassi, M. T.; Sperandeo, M. P.; Incerti, B; Bulfone, A; Pepe, A; Surace, Enrico Maria; Gattuso, C; De, Grandi; A, ; Buoninconti, A; Riboni, M; Manzoni, M; Andria, G; Ballabio, Andrea; Borsani, G; Sebastio, G.
TOWARDS CLINICAL TRIALS FOR AAV-MEDIATED EYE- AND LIVER - DIRECT GENE THERAPY TRANSLATION AAV
2011 Auricchio, Alberto; Surace, Enrico Maria; BRUNETTI PIERRI, Nicola
Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration.
2010 Simonelli, F; Maguire, Am; Testa, F; Pierce, Ea; Mingozzi, F; Bennicelli, Jl; Rossi, S; Marshall, K; Banfi, S; Surace, Enrico Maria; Sun, J; Redmond, Tm; Zhu, X; Shindler, Ks; Ying, Gs; Ziviello, C; Acerra, C; Wright, Jf; Mcdonnell, Jw; High, Ka; Bennett, J; Auricchio, Alberto
| Titolo | Tipologia | Data di pubblicazione | Autore(i) | File |
|---|---|---|---|---|
| Adeno-associated viral vectors for retinal gene transfer. | 1.1 Articolo in rivista | 2003 | Surace, Enrico Maria; Auricchio, Alberto | |
| The distribution, concentration, and toxicity of enhanced green fluorescent protein in retinal cells after genomic or somatic (virus-mediated) gene transfer. | 1.1 Articolo in rivista | 2005 | Rex, Ts; Peet, Ja; Surace, Enrico Maria; Calvert, Pd; Nikonov, Ss; Lyubarsky, Al; Bendo, E; Hughes, T; Pugh EN, Jr; Bennett, J. | |
| Localization of pigment epithelium derived factor (PEDF) in developing and adult human ocular tissues. | 1.1 Articolo in rivista | 2001 | Karakousis, Pc; John, Sk; Behling, Kc; Surace, Enrico Maria; Smith, Je; Hendrickson, A; Tang, Wx; Bennett, J; Milam, Ah | |
| Pigment epithelium-derived factor expression in the developing mouse eye. | 1.1 Articolo in rivista | 2002 | Behling, Kc; Surace, Enrico Maria; Bennett, J. | |
| Expression pattern of the ocular albinism type 1 (Oa1) gene in the murine retinal pigment epithelium. | 1.1 Articolo in rivista | 2000 | Surace, Enrico Maria; Angeletti, B; Ballabio, Andrea; Marigo, V. | |
| Oa1 knock-out: new insights on the pathogenesis of ocular albinism type 1 | 1.1 Articolo in rivista | 2000 | Incerti, B; Cortese, K; Pizzigoni, A; Surace, Enrico Maria; Varani, S; Coppola, M; Jeffery, G; Seeliger, M; Jaissle, G; Bennett, Dc; Marigo, V; Schiaffino, Mv; Tacchetti, C; Ballabio, Andrea | |
| The ocular albinism type 1 (OA1) protein, an intracellur G protein-coupled receptor, regulates melanosome transport in pigment cells. | 1.1 Articolo in rivista | 2008 | Palmisano, I; Bagnato, P; Palmigiano, A; Innamorati, P; Rotondo, G; Altimare, D; Venturi, C; Sviderskaya, Ev; Piccirillo, R; Coppola, M; Marigo, V; Incerti, B; Ballabio, Andrea; Surace, Enrico Maria; Tacchetti, C; Bennett, Dc; Schiaffino, M. V. | |
| AAV vectors efficiently and stably transduce fetal retina. | 1.1 Articolo in rivista | 2003 | Surace, Enrico Maria; Auricchio, Alberto; Reich, S. J.; Rex, T.; Glover, E.; Pineles, S.; Tang, W.; O’Connor, E.; Lyubarsky, A.; Savchenko, A.; Pugh, E.; Maguire, A. WILSON J. M. BENNETT J. | |
| Oa1 knock-out: new insights on the pathogenesis of ocular albinism type 1. | 1.1 Articolo in rivista | 2000 | Incerti, B; Cortese, K; Pizzigoni, A; Surace, Enrico Maria; Varani, S; Coppola, M; Jeffery, G; Seeliger, M; Jaissle, G; Bennett, Dc; Marigo, V; Schiaffino, Mv; Tacchetti, C; Ballabio, Andrea | |
| SLC7A8, a gene mapping within the lysinuric protein intolerance critical region, encodes a new member of the glycoprotein-associated amino acid transporter family. | 1.1 Articolo in rivista | 1999 | Bassi, Mt; Sperandeo, Mp; Incerti, B; Bulfone, A; Pepe, A; Surace, Enrico Maria; Gattuso, C; De Grandi, A; Buoninconti, A; Riboni, M; Manzoni, M; Andria, G; Ballabio, Andrea; Borsani, G; Sebastio, G. | |
| GENE THERAPY FOR LEBER'S CONGENITAL AMAUROSIS IS SAFE AND EFFECTIVE 1.5 YEARS AFTER VECTOR ADMINISTRATION | 1.1 Articolo in rivista | 2010 | F., Simonelli; A. M., Maguire; F., Testa; E. A., Pierce; F., Mingozzi; J. L., Bennicelli; S., Rossi; K., Marshall; S., Banfi; Surace, Enrico Maria; J., Sun; T. M., Redmond; X., Zhu; K. S., Scindler; G. S., Ying; C., Ziviello; C., Acerra; J. F., Wright; J. W., Mcdonnell; K. A., High; J., Bennett; Auricchio, Alberto | |
| Recombinant vectors based on porcine adeno-associated viral serotypes transduce the murine and pig retina. | 1.1 Articolo in rivista | 2013 | Puppo, A; Bello, A; Manfredi, A; Cesi, G; Marrocco, E; Della Corte, M; Rossi, S; Giunti, M; Bacci, Ml; Simonelli, F; Surace, Enrico Maria; Kobinger, Gp; Auricchio, Alberto | |
| Molecular and clinical characterization of albinism in a large cohort of Italian patients. | 1.1 Articolo in rivista | 2011 | Gargiulo, A; Testa, F; Rossi, S; Di Iorio, V; Fecarotta, S; DE BERARDINIS, Teresa; Iovine, A; Magli, A; Signorini, S; Fazzi, E; Galantuomo, Ms; Fossarello, M; Montefusco, S; Ciccodicola, A; Neri, A; Macaluso, C; Simonelli, F; Surace, Enrico Maria | |
| Three-year follow-up after unilateral subretinal delivery of adeno-associated virus in patients with Leber congenital Amaurosis type 2. | 1.1 Articolo in rivista | 2013 | Testa, F; Maguire, Am; Rossi, S; Pierce, Ea; Melillo, P; Marshall, K; Banfi, S; Surace, Enrico Maria; Sun, J; Acerra, C; Wright, Jf; Wellman, J; High, Ka; Auricchio, Alberto; Bennett, J; Simonelli, F. | |
| The long noncoding RNA Vax2os1 controls the cell cycle progression of photoreceptor progenitors in the mouse retina. | 1.1 Articolo in rivista | 2012 | Meola, N; Pizzo, M; Alfano, G; Surace, Enrico Maria; Banfi, S. | |
| Delivery of adeno-associated virus vectors to the fetal retina: impact of viral capsid proteins on retinal neuronal progenitor transduction. | 1.1 Articolo in rivista | 2003 | Surace, Enrico Maria; Auricchio, Alberto; Reich, Sj; Rex, T; Glover, E; Pineles, S; Tang, W; O'Connor, E; Lyubarsky, A; Savchenko, A; Pugh EN, Jr; Maguire, Am; Wilson, Jm; Bennett, J. | |
| Systemic but not intraocular Epo gene transfer protects the retina from light- and genetic-induced degeneration. | 1.1 Articolo in rivista | 2004 | Rex, T. S.; M. ALLOCCA, M.; Domenici, L.; Surace, Enrico Maria; Maguire, A. M.; Lyubarsky, A.; Cellerino, A.; Bennett, J.; Auricchio, Alberto | |
| SLC7A8, a gene mapping within the lysinuric protein intolerance critical region, encodes a new member of the glycoprotein associated amino acid transporter family. | 1.1 Articolo in rivista | 1999 | Bassi, M. T.; Sperandeo, M. P.; Incerti, B; Bulfone, A; Pepe, A; Surace, Enrico Maria; Gattuso, C; De, Grandi; A, ; Buoninconti, A; Riboni, M; Manzoni, M; Andria, G; Ballabio, Andrea; Borsani, G; Sebastio, G. | |
| TOWARDS CLINICAL TRIALS FOR AAV-MEDIATED EYE- AND LIVER - DIRECT GENE THERAPY TRANSLATION AAV | 8.07 Progetti di Ricerca Finanziati | 2011 | Auricchio, Alberto; Surace, Enrico Maria; BRUNETTI PIERRI, Nicola | |
| Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration. | 1.1 Articolo in rivista | 2010 | Simonelli, F; Maguire, Am; Testa, F; Pierce, Ea; Mingozzi, F; Bennicelli, Jl; Rossi, S; Marshall, K; Banfi, S; Surace, Enrico Maria; Sun, J; Redmond, Tm; Zhu, X; Shindler, Ks; Ying, Gs; Ziviello, C; Acerra, C; Wright, Jf; Mcdonnell, Jw; High, Ka; Bennett, J; Auricchio, Alberto |