SURACE, Enrico Maria

SURACE, Enrico Maria  

DIPARTIMENTO DI SCIENZE MEDICHE TRASLAZIONALI  

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Adeno-associated viral vectors for retinal gene transfer. 1.1 Articolo in rivista 2003 Surace, Enrico Maria; Auricchio, Alberto
The distribution, concentration, and toxicity of enhanced green fluorescent protein in retinal cells after genomic or somatic (virus-mediated) gene transfer. 1.1 Articolo in rivista 2005 Rex, Ts; Peet, Ja; Surace, Enrico Maria; Calvert, Pd; Nikonov, Ss; Lyubarsky, Al; Bendo, E; Hughes, T; Pugh EN, Jr; Bennett, J.
Localization of pigment epithelium derived factor (PEDF) in developing and adult human ocular tissues. 1.1 Articolo in rivista 2001 Karakousis, Pc; John, Sk; Behling, Kc; Surace, Enrico Maria; Smith, Je; Hendrickson, A; Tang, Wx; Bennett, J; Milam, Ah
Pigment epithelium-derived factor expression in the developing mouse eye. 1.1 Articolo in rivista 2002 Behling, Kc; Surace, Enrico Maria; Bennett, J.
Expression pattern of the ocular albinism type 1 (Oa1) gene in the murine retinal pigment epithelium. 1.1 Articolo in rivista 2000 Surace, Enrico Maria; Angeletti, B; Ballabio, Andrea; Marigo, V.
Oa1 knock-out: new insights on the pathogenesis of ocular albinism type 1 1.1 Articolo in rivista 2000 Incerti, B; Cortese, K; Pizzigoni, A; Surace, Enrico Maria; Varani, S; Coppola, M; Jeffery, G; Seeliger, M; Jaissle, G; Bennett, Dc; Marigo, V; Schiaffino, Mv; Tacchetti, C; Ballabio, Andrea
Combined rod and cone transduction by AAV2/8. 1.1 Articolo in rivista 2013 Manfredi, A; Marrocco, E; Puppo, A; Cesi, G; Sommella, A; Della Corte, M; Rossi, S; Giunti, M; Craft, Cm; Bacci, Ml; Simonelli, F; Surace, Enrico Maria; Auricchio, Alberto
Transdermal spinal catheter placement in piglets: Description and validation of the technique. 1.1 Articolo in rivista 2015 Lambertini, C; Ventrella, D; Barone, F; Sorrentino, Nc; Dondi, F; Fraldi, Alessandro; Giunti, M; Surace, Enrico Maria; Bacci, Ml; Romagnoli, N.
Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial. 1.1 Articolo in rivista 2009 Maguire, Am; High, Ka; Auricchio, Alberto; Wright, Jf; Pierce, Ea; Testa, F; Mingozzi, F; Bennicelli, Jl; Ying, Gs; Rossi, S; Fulton, A; Marshall, Ka; Banfi, S; Chung, Dc; Morgan, Ji; Hauck, B; Zelenaia, O; Zhu, X; Raffini, L; Coppieters, F; De Baere, E; Shindler, Ks; Volpe, Nj; Surace, Enrico Maria; Acerra, C; Lyubarsky, A; Redmond, Tm; Stone, E; Sun, J; Mcdonnell, Jw; Leroy, Bp; Simonelli, F; Bennett, J.
Phenotypic rescue after adeno-associated virus-mediated delivery of 4-sulfatase to the retinal pigment epithelium of feline mucopolysaccharidosis VI. 1.1 Articolo in rivista 2002 Ho, Tt; Maguire, Am; Aguirre, Gd; Surace, Enrico Maria; Anand, V; Zeng, Y; Salvetti, A; Hopwood, Jj; Haskins, Me; Bennett, J.
SLC7A8, a gene mapping within the lysinuric protein intolerance critical region, encodes a new member of the glycoprotein-associated amino acid transporter family. 1.1 Articolo in rivista 1999 Bassi, Mt; Sperandeo, Mp; Incerti, B; Bulfone, A; Pepe, A; Surace, Enrico Maria; Gattuso, C; De Grandi, A; Buoninconti, A; Riboni, M; Manzoni, M; Andria, G; Ballabio, Andrea; Borsani, G; Sebastio, G.
Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration. 1.1 Articolo in rivista 2010 Simonelli, F; Maguire, Am; Testa, F; Pierce, Ea; Mingozzi, F; Bennicelli, Jl; Rossi, S; Marshall, K; Banfi, S; Surace, Enrico Maria; Sun, J; Redmond, Tm; Zhu, X; Shindler, Ks; Ying, Gs; Ziviello, C; Acerra, C; Wright, Jf; Mcdonnell, Jw; High, Ka; Bennett, J; Auricchio, Alberto
Inhibition of ocular neovascularization by Hedgehog blockade. 1.1 Articolo in rivista 2006 Surace, Enrico Maria; Balaggan, K. S.; Tessitore, A.; Mussolino, C.; Cotugno, G.; Bonetti, C.; Vitale, A.; Ali, R. R.; Auricchio, Alberto
AP20817-inducible activation of chimeric insulin receptor mimics insulin action in hepatocytes transduced with AAV 4.1 Articoli in Atti di convegno 2004 Auricchio, Alberto; G., Cotugno; Formisano, Pietro; Beguinot, Francesco; Surace, Enrico Maria; R., Pollock
Amelioration of both functional and morphological abnormalities in the retina of a mouse model of ocular albinism following AAV-mediated gene transfer. 1.1 Articolo in rivista 2005 Surace, Enrico Maria; Domenici, L; Cortese, K; Cotugno, G; Di Vicino, U; Venturi, C; Cellerino, A; Marigo, V; Tacchetti, C; Ballabio, Andrea; Auricchio, Alberto
The ocular albinism type 1 protein, an intracellular G protein-coupled receptor, regulates melanosome transport in pigment cells. 1.1 Articolo in rivista 2008 Palmisano, I; Bagnato, P; Palmigiano, A; Innamorati, G; Rotondo, G; Altimare, D; Venturi, C; Sviderskaya, Ev; Piccirillo, R; Coppola, M; Marigo, V; Incerti, B; Ballabio, Andrea; Surace, Enrico Maria; Tacchetti, C; Bennett, Dc; Schiaffino, Mv
Systemic but not intraocular Epo gene transfer protects the retina from light- and genetic-induced degeneration. 1.1 Articolo in rivista 2004 Rex, T. S.; M. ALLOCCA, M.; Domenici, L.; Surace, Enrico Maria; Maguire, A. M.; Lyubarsky, A.; Cellerino, A.; Bennett, J.; Auricchio, Alberto
Versatility of AAV vectors for retinal gene transfer 1.1 Articolo in rivista 2008 Surace, Enrico Maria; Auricchio, Alberto
The ocular albinism type 1 (OA1) protein, an intracellur G protein-coupled receptor, regulates melanosome transport in pigment cells. 1.1 Articolo in rivista 2008 Palmisano, I; Bagnato, P; Palmigiano, A; Innamorati, P; Rotondo, G; Altimare, D; Venturi, C; Sviderskaya, Ev; Piccirillo, R; Coppola, M; Marigo, V; Incerti, B; Ballabio, Andrea; Surace, Enrico Maria; Tacchetti, C; Bennett, Dc; Schiaffino, M. V.
SLC7A8, a gene mapping within the lysinuric protein intolerance critical region, encodes a new member of the glycoprotein associated amino acid transporter family. 1.1 Articolo in rivista 1999 Bassi, M. T.; Sperandeo, M. P.; Incerti, B; Bulfone, A; Pepe, A; Surace, Enrico Maria; Gattuso, C; De, Grandi; A, ; Buoninconti, A; Riboni, M; Manzoni, M; Andria, G; Ballabio, Andrea; Borsani, G; Sebastio, G.