Similar Therapeutic Efficacy Between a Single Administration of Gene Therapy and Multiple Administrations of Recombinant Enzyme in a Mouse Model of Lysosomal Storage Disease / Ferla, R; Claudiani, P; Cotugno, G; Saccone, P; De Leonibus, E; Auricchio, Alberto. - In: HUMAN GENE THERAPY. - ISSN 1043-0342. - (2014). [10.1089/hum.2013.213]
Similar Therapeutic Efficacy Between a Single Administration of Gene Therapy and Multiple Administrations of Recombinant Enzyme in a Mouse Model of Lysosomal Storage Disease.
AURICCHIO, ALBERTO
2014
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