AURICCHIO, ALBERTO

AURICCHIO, ALBERTO  

DIPARTIMENTO DI SCIENZE BIOMEDICHE AVANZATE  

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Efficient trans-splicing in the retina expands the utility of adeno-associated virus as a vector for gene therapy. 1.1 Articolo in rivista 2003 Reich, S. J.; Auricchio, Alberto; Hildinger, M.; Glover, E.; Maguire, A. M.; Wilson, J. M.; Bennett, J.
Constitutive and regulated expression of processed insulin following in vivo hepatic gene transfer. 1.1 Articolo in rivista 2002 Auricchio, Alberto; Gao, G. P.; Yu, Q. C.; Raper, S.; Rivera, V.; Wilson, J. M.
A single-step affinity column for purification of serotype 5-based adeno-associated viral vectors. 1.1 Articolo in rivista 2001 Auricchio, Alberto; CONNOR E., O’; Hildinger, M.; Wilson, J. M.
Pharmacologically-regulated gene expression in the retina following transduction with viral vectors. 1.1 Articolo in rivista 2001 Dejneka, N.; Auricchio, Alberto; Maguire, A.; Ye, X.; Gao, G. P.; Wilson, J. M. W.; Bennett, J.
Hybrid vectors based on adeno-associated virus serotype 2 and 5 for muscle directed gene transfer. 1.1 Articolo in rivista 2001 Hildinger, M.; Auricchio, Alberto; Gao, G. P.; Wang, L.; Chirmule, N.; Wilson, J. M.
Exchange of surface proteins impacts on viral vector cellular specificity and transduction characteristics: the retina as a model. 1.1 Articolo in rivista 2001 Auricchio, Alberto; Kobinger, G.; Anand, V.; Hildinger, M.; CONNOR E., O’; Maguire, A.; Wilson, J. M.; Bennett, J.
Autonomic dysfunction in children with Hirschsprung's disease. 1.1 Articolo in rivista 1999 Staiano, Annamaria; Santoro, L.; DE MARCO, R.; Miele, Erasmo; Fiorillo, F.; Auricchio, Alberto; Carpentieri, M. L.; Auricchio, S.
Endothelin-B receptor mutations in patients with isolated Hirschsprung disease from a non inbred population. 1.1 Articolo in rivista 1996 Auricchio, Alberto; Casari, G.; Staiano, Annamaria; Ballabio, Andrea
Adeno-associated viral vectors for retinal gene transfer. 1.1 Articolo in rivista 2003 Surace, Enrico Maria; Auricchio, Alberto
Identification and biochemical characterization of novel putative substrates for the Epidermal Growth Factor Receptor kinase. 1.1 Articolo in rivista 1992 Fazioli, F.; Bottaro, D. P.; Minichiello, L.; Auricchio, Alberto
AAV-mediated gene transfer for retinal diseases 8.02 Comunicazioni a Convegni o Seminari 2006 Auricchio, Alberto
Microphthalmia transcription factor controls expression of the Ocular albinism type 1 gene. 1.1 Articolo in rivista 2004 Vetrini, F.; Auricchio, Alberto; Du, J.; Angeletti, B.; Fisherl, D. E.; Ballabio, Andrea; Marigo, V.
Effect of over-expression of Pigment Epithelium-Derived Factor (PEDF) on developing retinal vasculature in the mouse. 1.1 Articolo in rivista 2004 Wong, W. T.; Rex, T. S.; Auricchio, Alberto; Maguire, A. M.; Chung, D.; Tang, W.; Bennett, J.
An in vivo doxycycline-controlled expression system for functional studies of the retina. 1.1 Articolo in rivista 2003 Angeletti, B; Loster, J; Auricchio, Alberto; Gekeler, F; Shinoda, K; Ballabio, Andrea; Graw, J; Marigo, V.
Double heterozygosity for a RET substitution interfering with splicing and an EDNRB missense mutation in Hirschsprung disease. 1.1 Articolo in rivista 1999 Auricchio, Alberto; Griseri, P; Carpentieri, M. L.; Betsos, N; Staiano, Annamaria; Tozzi, A; Priolo, M; Thompson, H; Bocciardi, R; Romeo, G; Ballabio, Andrea; Ceccherini, I.
Endothelin-B receptor mutations in patients with isolated Hirschsprung disease from a non-inbred population. 1.1 Articolo in rivista 1996 Auricchio, Alberto; Casari, G; Staiano, Annamaria; Ballabio, Andrea
Correction of Hunter syndrome via gene delivery using the MPSII mouse model. 1.1 Articolo in rivista 2006 Cardone, M.; Polito, V. A.; Pepe, S.; Dazzo, A.; Muenzer, J.; Auricchio, Alberto; Ballabio, Andrea; Cosma, M. P. .
associate editoe 8.06 Partecip. Editorial Board di riviste scientifiche 2008 Auricchio, Alberto
Tissue engineering with viral vectors to produce secreted proteins for metabolic diseases 8.07 Progetti di Ricerca Finanziati 2005 Auricchio, Alberto
Gene Therapy for Diabetic Retinopathy 8.02 Comunicazioni a Convegni o Seminari 2002 Auricchio, Alberto