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Titolo Tipologia Data di pubblicazione Autore(i) File
Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial. 1.1 Articolo in rivista 2009 Maguire, Am; High, Ka; Auricchio, Alberto; Wright, Jf; Pierce, Ea; Testa, F; Mingozzi, F; Bennicelli, Jl; Ying, Gs; Rossi, S; Fulton, A; Marshall, Ka; Banfi, S; Chung, Dc; Morgan, Ji; Hauck, B; Zelenaia, O; Zhu, X; Raffini, L; Coppieters, F; De Baere, E; Shindler, Ks; Volpe, Nj; Surace, Enrico Maria; Acerra, C; Lyubarsky, A; Redmond, Tm; Stone, E; Sun, J; Mcdonnell, Jw; Leroy, Bp; Simonelli, F; Bennett, J.
AAV-mediated Tyrosinase Gene Transfer Restores Melanogenesis and Retinal Function in a Model of Oculo-cutaneous Albinism Type I (OCA1). 1.1 Articolo in rivista 2009 A., Gargiulo; C., Bonetti; S., Montefusco; S., Neglia; U., Di Vicino; E., Marrocco; Md, Corte; L., Domenici; Auricchio, Alberto; Surace, Enrico Maria
The ocular albinism type 1 (OA1) protein, an intracellur G protein-coupled receptor, regulates melanosome transport in pigment cells. 1.1 Articolo in rivista 2008 Palmisano, I; Bagnato, P; Palmigiano, A; Innamorati, P; Rotondo, G; Altimare, D; Venturi, C; Sviderskaya, Ev; Piccirillo, R; Coppola, M; Marigo, V; Incerti, B; Ballabio, Andrea; Surace, Enrico Maria; Tacchetti, C; Bennett, Dc; Schiaffino, M. V.
The ocular albinism type 1 protein, an intracellular G protein-coupled receptor, regulates melanosome transport in pigment cells. 1.1 Articolo in rivista 2008 Palmisano, I; Bagnato, P; Palmigiano, A; Innamorati, G; Rotondo, G; Altimare, D; Venturi, C; Sviderskaya, Ev; Piccirillo, R; Coppola, M; Marigo, V; Incerti, B; Ballabio, Andrea; Surace, Enrico Maria; Tacchetti, C; Bennett, Dc; Schiaffino, Mv
Safety and efficacy of gene transfer for Leber's congenital amaurosis. 1.1 Articolo in rivista 2008 Maguire, Am; Simonelli, F; Pierce, Ea; Pugh EN, Jr; Mingozzi, F; Bennicelli, J; Banfi, S; Marshall, Ka; Testa, F; Surace, Enrico Maria; Rossi, S; Lyubarsky, A; Arruda, Vr; Konkle, B; Stone, E; Sun, J; Jacobs, J; Dell'Osso, L; Hertle, R; Ma, Jx; Redmond, Tm; Zhu, X; Hauck, B; Zelenaia, O; Shindler, Ks; Maguire, Mg; Wright, Jf; Volpe, Nj; Mcdonnell, Jw; Auricchio, Alberto; High, Ka; Bennett, J.
Versatility of AAV vectors for retinal gene transfer 1.1 Articolo in rivista 2008 Surace, Enrico Maria; Auricchio, Alberto
Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors. 1.1 Articolo in rivista 2007 Allocca, M; Mussolino, C; Garcia Hoyos, M; Sanges, D; Iodice, C; Petrillo, M; Vandenberghe, Lh; Wilson, Jm; Marigo, V; Surace, Enrico Maria; Auricchio, Alberto
Sulfatase modifying factor 1 trafficking through the cells: from endoplasmic reticulum to the endoplasmic reticulum. 1.1 Articolo in rivista 2007 Zito, E; Buono, M; Pepe, S; Settembre, Carmine; Annunziata, I; Surace, Enrico Maria; Dierks, T; Monti, Maria; Cozzolino, M; Pucci, Pietro; Ballabio, Andrea; Cosma, Mp
Aberrant splicing in the ocular albinism type 1 gene (OA1/GPR143) is corrected in vitro by morpholino antisense oligonucleotides. 1.1 Articolo in rivista 2006 Vetrini, F; Tammaro, R; Bondanza, S; Surace, Enrico Maria; Auricchio, Alberto; De Luca, M; Ballabio, Andrea; Marigo, V.
Inhibition of ocular neovascularization by Hedgehog blockade. 1.1 Articolo in rivista 2006 Surace, Enrico Maria; Balaggan, K. S.; Tessitore, A.; Mussolino, C.; Cotugno, G.; Bonetti, C.; Vitale, A.; Ali, R. R.; Auricchio, Alberto
The distribution, concentration, and toxicity of enhanced green fluorescent protein in retinal cells after genomic or somatic (virus-mediated) gene transfer. 1.1 Articolo in rivista 2005 Rex, Ts; Peet, Ja; Surace, Enrico Maria; Calvert, Pd; Nikonov, Ss; Lyubarsky, Al; Bendo, E; Hughes, T; Pugh EN, Jr; Bennett, J.
Use of compounds that interfere with the hedghehog signaling pathway for the manufacture of a medicament for preventing, inhibiting 6.1 Brevetto 2005 Auricchio, A; Hildinger, M; Surace, ENRICO MARIA
Amelioration of both functional and morphological abnormalities in the retina of a mouse model of ocular albinism following AAV-mediated gene transfer. 1.1 Articolo in rivista 2005 Surace, Enrico Maria; Domenici, L; Cortese, K; Cotugno, G; Di Vicino, U; Venturi, C; Cellerino, A; Marigo, V; Tacchetti, C; Ballabio, Andrea; Auricchio, Alberto
The Ocular Albinism type 1 (OA!) gene controls melanosome maturation and size. 1.1 Articolo in rivista 2005 Cortese, K; Giordano, F; Surace, Enrico Maria; Venturi, C; Ballabio, Andrea; Tacchetti, C; AND MARIGO, V.
The ocular albinism type 1 (OA1) gene controls melanosome maturation and size. 1.1 Articolo in rivista 2005 Cortese, K; Giordano, F; Surace, Enrico Maria; Venturi, C; Ballabio, Andrea; Tacchetti, C; Marigo, V.
Systemic but not intraocular Epo gene transfer protects the retina from light- and genetic-induced degeneration. 1.1 Articolo in rivista 2004 Rex, T. S.; M. ALLOCCA, M.; Domenici, L.; Surace, Enrico Maria; Maguire, A. M.; Lyubarsky, A.; Cellerino, A.; Bennett, J.; Auricchio, Alberto
In utero gene therapy rescues vision in a murine model of congenital blindness. 1.1 Articolo in rivista 2004 Dejneka, Ns; Surace, Enrico Maria; Aleman, Ts; Cideciyan, Av; Lyubarsky, A; Savchenko, A; Redmond, Tm; Tang, W; Wei, Z; Rex, Ts; Glover, E; Maguire, Am; Pugh EN, Jr; Jacobson, Sg; Bennett, J.
Systemic but not intraocular Epo gene transfer protects the retina from light-and genetic-induced degeneration. 1.1 Articolo in rivista 2004 Rex, Ts; Allocca, M; Domenici, L; Surace, Enrico Maria; Maguire, Am; Lyubarsky, A; Cellerino, A; Bennett, J; Auricchio, Alberto
AP20817-inducible activation of chimeric insulin receptor mimics insulin action in hepatocytes transduced with AAV 4.1 Articoli in Atti di convegno 2004 Auricchio, Alberto; G., Cotugno; Formisano, Pietro; Beguinot, Francesco; Surace, Enrico Maria; R., Pollock
Adeno-associated viral vectors for retinal gene transfer. 1.1 Articolo in rivista 2003 Surace, Enrico Maria; Auricchio, Alberto
Mostrati risultati da 41 a 60 di 72
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