Trapani, Ivana

Trapani, Ivana  

DIPARTIMENTO DI SCIENZE BIOMEDICHE AVANZATE  

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Titolo Tipologia Data di pubblicazione Autore(i) File
Gene Therapy of ABCA4-Associated Diseases. 1.1 Articolo in rivista 2015 Auricchio, Alberto; Trapani, I; Allikmets, R.
Efficient gene delivery to the cone-enriched pig retina by dual AAV vectors. 1.1 Articolo in rivista 2014 Colella, P; Trapani, I; Cesi, G; Sommella, A; Manfredi, A; Puppo, A; Iodice, C; Rossi, S; Simonelli, F; Giunti, M; Bacci, Ml; Auricchio, Alberto
Effective delivery of large genes to the retina by dual AAV vectors. 1.1 Articolo in rivista 2013 Trapani, I; Colella, P; Sommella, A; Iodice, C; Cesi, G; De Simone, S; Marrocco, E; Rossi, S; Giunti, M; Palfi, A; Jane Farrar, G; Polishchuk, R; Auricchio, Alberto
Vector platforms for gene therapy of inherited retinopathies. 1.1 Articolo in rivista 2014 Trapani, I; Puppo, A; Auricchio, Alberto
Improved dual AAV vectors with reduced expression of truncated proteins are safe and effective in the retina of a mouse model of Stargardt disease 1.1 Articolo in rivista 2015 Trapani, Ivana; Toriello, Elisabetta; de Simone, Sonia; Colella, Pasqualina; Iodice, Carolina; Polishchuk, Elena V; Sommella, Andrea; Colecchi, Linda; Rossi, Settimio; Simonelli, Francesca; Giunti, Massimo; Bacci, Maria L; Polishchuk, Roman S; Auricchio, Alberto
Seeing the Light after 25 Years of Retinal Gene Therapy 1.1 Articolo in rivista 2018 Trapani, Ivana; Auricchio, Alberto
Has retinal gene therapy come of age? From bench to bedside and back to bench 1.1 Articolo in rivista 2019 Trapani, Ivana; Auricchio, Alberto
Treatment of bone growth disorders 6.1 Brevetto 2016 Settembre, Carmine; Cinque, Laura; Bartolomeo, Rosa; Auricchio, Alberto; Trapani, Ivana; Toriello, Elisabetta
Multiple vector system and uses thereof. 6.1 Brevetto 2015 Colella, P; Auricchio, A; Trapani, I
Effective delivery of large genes by dual vectors 6.1 Brevetto 2013 Auricchio, A; Colella, P; Trapani, I
Intein-mediated protein trans-splicing expands adeno-associated virus transfer capacity in the retina 1.1 Articolo in rivista 2019 Tornabene, Patrizia; Trapani, I.; Minopoli, R.; Centrulo, M.; Lupo, M.; De Simone, S.; Tiberi, Mario; Dell'Aquila, F.; Marrocco, E.; Iodice, C.; Iuliano, A.; Gesualdo, C.; Rossi, S.; Giaquinto, L.; Albert, S.; Hoyng, C. B.; Polishchuk, E.; Cremers, F. P. M.; Surace, E. M.; Simonelli, F.; De Matteis, M. A.; Polishchuk, R.; Auricchio, A.
Gene therapy of inherited retinal degenerations: prospects and challenges. 1.1 Articolo in rivista 2015 Trapani, I; Banfi, S; Simonelli, F; Surace, Enrico Maria; Auricchio, Alberto
Inclusion of a degron reduces levelsof undesired inteins after AAV-mediated proteintrans-splicing in the retina 1.1 Articolo in rivista 2021 Tornabene, P.; Trapani, I.; Centrulo, M.; Marrocco, E.; Minopoli, R.; Lupo, M.; Iodice, C.; Gesualdo, C.; Simonelli, F.; Surace, E. M.; Auricchio, A.
Large gene delivery to the retina with AAV vectors: are we there yet? 1.1 Articolo in rivista 2021 Trapani, I.; Tornabene, P.; Auricchio, A.
Dual AAV vectors for stargardt disease 2.1 Contributo in volume (Capitolo o Saggio) 2018 Trapani, I.
Can Adeno-Associated Viral Vectors Deliver Effectively Large Genes? 1.2 Recensione in rivista 2020 Tornabene, P; Trapani, I
Adeno-associated viral vectors as a tool for large gene delivery to the retina 1.2 Recensione in rivista 2019 Trapani, I.
The Opportunities and Challenges of Gene Therapy for Treatment of Inherited Forms of Vision and Hearing Loss 1.8 Articolo in rassegna (review) 2023 Simons, E. J.; Trapani, I.
A new age of precision gene therapy 1.8 Articolo in rassegna (review) 2024 Schambach, A.; Buchholz, C. J.; Torres-Ruiz, R.; Cichutek, K.; Morgan, M.; Trapani, I.; Buning, H.
Light-responsive microRNA miR-211 targets Ezrin to modulate lysosomal biogenesis and retinal cell clearance 1.1 Articolo in rivista 2020 Naso, Federica; Intartaglia, Daniela; Falanga, Danila; Soldati, Chiara; Polishchuk, Elena; Giamundo, Giuliana; Tiberi, Paola; Marrocco, Elena; Scudieri, Paolo; Di Malta, Chiara; Trapani, Ivana; Nusco, Edoardo; Salierno, Francesco Giuseppe; Surace, Enrico Maria; Galietta, Luis Jv; Banfi, Sandro; Auricchio, Alberto; Ballabio, Andrea; Medina, Diego Luis; Conte, Ivan