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Functional restoration of a CFTR splicing mutation through RNA delivery of CRISPR adenine base editor 1.1 Articolo in rivista 2023 Amistadi, Simone; Maule, Giulia; Ciciani, Matteo; Ensinck, Marjolein M; De Keersmaecker, Liesbeth; Ramalho, Anabela S; Guidone, Daniela; Buccirossi, Martina; Galietta, Luis Juan Vicente; Carlon, Marianne S; Cereseto, Anna
Putting bicarbonate on the spot: pharmacological insights for CFTR correction in the airway epithelium 1.1 Articolo in rivista 2023 Zajac, Miroslaw; Lepissier, Agathe; Dréano, Elise; Chevalier, Benoit; Hatton, Aurélie; Kelly-Aubert, Mairead; Guidone, Daniela; Planelles, Gabrielle; Edelman, Aleksander; Girodon, Emmanuelle; Hinzpeter, Alexandre; Crambert, Gilles; Pranke, Iwona; Galietta, Luis Juan Vicente; Sermet-Gaudelus, Isabelle
Easy-to-Build and Reusable Microfluidic Device for the Dynamic Culture of Human Bronchial Cystic Fibrosis Epithelia 1.1 Articolo in rivista 2023 Mazio, Claudia; Scognamiglio, Laura S; Passariello, Roberta; Panzetta, Valeria; Casale, Costantino; Urciuolo, Francesco; Galietta, Luis Juan Vicente; Imparato, Giorgia; Netti, Paolo A
Novel tricyclic pyrrolo-quinolines as pharmacological correctors of the mutant CFTR chloride channel 1.1 Articolo in rivista 2023 Renda, Mario; Barreca, Marilia; Borrelli, Anna; Spanò, Virginia; Montalbano, Alessandra; Raimondi, Maria Valeria; Bivacqua, Roberta; Musante, Ilaria; Scudieri, Paolo; Guidone, Daniela; Buccirossi, Martina; Genovese, Michele; Venturini, Arianna; Bandiera, Tiziano; Barraja, Paola; Galietta, Luis Juan Vicente
Pharmacological potentiators of the calcium signaling cascade identified by high-throughput screening 1.1 Articolo in rivista 2022 Genovese, Michele; Guidone, Daniela; Buccirossi, Martina; Borrelli, Anna; Rodriguez-Gimeno, Alejandra; Bertozzi, Fabio; Bandiera, Tiziano; Galietta, Luis Juan Vicente
Isolation, cultivation, and application of primary respiratory epithelial cells obtained by nasal brushing, polyp samples, or lung explants 1.1 Articolo in rivista 2022 Golec, Anita; Pranke, Iwona; Scudieri, Paolo; Hayes, Kate; Dreano, Elise; Dunlevy, Fiona; Hatton, Aurelie; Downey, Damian G; Galietta, Luis; Sermet, Isabelle
Airway surface hyperviscosity and defective mucociliary transport by IL-17/TNF-α are corrected by beta-adrenergic stimulus 1.1 Articolo in rivista 2022 Guidone, Daniela; Buccirossi, Martina; Scudieri, Paolo; Genovese, Michele; Sarnataro, Sergio; De Cegli, Rossella; Cresta, Federico; Terlizzi, Vito; Planelles, Gabrielle; Crambert, Gilles; Sermet-Gaudelus, Isabelle; Galietta, Luis Jv
TMEM16A (ANO1) as a therapeutic target in cystic fibrosis 1.2 Recensione in rivista 2022 Galietta, L
Rescue by elexacaftor-tezacaftor-ivacaftor of the G1244E cystic fibrosis mutation's stability and gating defects are dependent on cell background 1.1 Articolo in rivista 2022 Tomati, Valeria; Costa, Stefano; Capurro, Valeria; Pesce, Emanuela; Pastorino, Cristina; Lena, Mariateresa; Sondo, Elvira; Di Duca, Marco; Cresta, Federico; Cristadoro, Simona; Zara, Federico; Galietta, Luis Juan Vicente; Bocciardi, Renata; Castellani, Carlo; Lucanto, Maria Cristina; Pedemonte, Nicoletta
Esc peptides as novel potentiators of defective cystic fibrosis transmembrane conductance regulator: an unprecedented property of antimicrobial peptides 1.1 Articolo in rivista 2022 Ferrera, L.; Cappiello, F.; Loffredo, M. R.; Puglisi, E.; Casciaro, B.; Botta, B.; Galietta, L. J. V.; Mori, M.; Mangoni, M. L.
The L467F-F508del Complex Allele Hampers Pharmacological Rescue of Mutant CFTR by Elexacaftor/Tezacaftor/Ivacaftor in Cystic Fibrosis Patients: The Value of the Ex Vivo Nasal Epithelial Model to Address Non-Responders to CFTR-Modulating Drugs 1.1 Articolo in rivista 2022 Sondo, Elvira; Cresta, Federico; Pastorino, Cristina; Tomati, Valeria; Capurro, Valeria; Pesce, Emanuela; Lena, Mariateresa; Iacomino, Michele; Baffico, Ave Maria; Coviello, Domenico; Bandiera, Tiziano; Zara, Federico; Galietta, L; Bocciardi, Renata; Castellani, Carlo; Pedemonte, Nicoletta
KCa3.1 differentially regulates trachea and bronchi epithelial gene expression in a chronic-asthma mouse model 1.1 Articolo in rivista 2022 Philp, Amber R; Miranda, Fernando; Gianotti, Ambra; Mansilla, Agustín; Scudieri, Paolo; Musante, Ilaria; Vega, Génesis; Figueroa, Carlos D; Galietta, L; Sarmiento, José M; Flores, Carlos A
Analysis of inhibitors of the anoctamin-1 chloride channel (transmembrane member 16A, TMEM16A) reveals indirect mechanisms involving alterations in calcium signalling 1.1 Articolo in rivista 2022 Genovese, Michele; Buccirossi, Martina; Guidone, Daniela; De Cegli, Rossella; Sarnataro, Sergio; di Bernardo, Diego; Galietta, Luis J V
Comprehensive analysis of combinatorial pharmacological treatments to correct nonsense mutations in the cftr gene 1.1 Articolo in rivista 2021 Venturini, A.; Borrelli, A.; Musante, I.; Scudieri, P.; Capurro, V.; Renda, M.; Pedemonte, N.; Galietta, L. J. V.
Evaluation of Fused Pyrrolothiazole Systems as Correctors of Mutant CFTR Protein 1.1 Articolo in rivista 2021 Spano, V.; Barreca, M.; Cilibrasi, V.; Genovese, M.; Renda, M.; Montalbano, A.; Galietta, L. J. V.; Barraja, P.
Chloride transport modulators as drug candidates 1.1 Articolo in rivista 2021 Verkman, Alan S; Galietta, L
Pharmacological approaches to cystic fibrosis 1.1 Articolo in rivista 2021 Bandiera, T.; Galietta, L. J. V.
Partial rescue of f508del-cftr stability and trafficking defects by double corrector treatment 1.1 Articolo in rivista 2021 Capurro, V.; Tomati, V.; Sondo, E.; Renda, M.; Borrelli, A.; Pastorino, C.; Guidone, D.; Venturini, A.; Giraudo, A.; Bertozzi, S. M.; Musante, I.; Bertozzi, F.; Bandiera, T.; Zara, F.; Galietta, L. J. V.; Pedemonte, N.
Ex vivo model predicted in vivo efficacy of CFTR modulator therapy in a child with rare genotype 1.1 Articolo in rivista 2021 Terlizzi, V.; Amato, F.; Castellani, C.; Ferrari, B.; Galietta, L. J. V.; Castaldo, G.; Taccetti, G.
Pharmacoproteomics pinpoints HSP70 interaction for correction of the most frequent Wilson disease-causing mutant of ATP7B 1.1 Articolo in rivista 2020 Concilli, M.; Petruzzelli, R.; Parisi, S.; Catalano, F.; Sirci, F.; Napolitano, F.; Renda, M.; Galietta, L. J. V.; Bernardo, D. D.; Polishchuk, R. S.
Mostrati risultati da 1 a 20 di 183
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